Genetics & Genomics
Genetics & Genomics
Briefings on gene therapy, genomics, and rare-disease genetics — each summary tied to the study it came from.
A landmark trial used CRISPR-Cas9 to reactivate fetal hemoglobin in patients' own blood stem cells, freeing a sickle cell and a beta-thalassemia patient from crises and transfusions — and hinting at a pattern reused across blood disorders.